The treatment uses a modified, harmless virus to deliver healthy genes to a patient’s cells to treat genetic diseases. Read more at straitstimes.com. Read more at straitstimes.com.

Kerala doctors successfully performed a life-saving liver transplant on a two-and-a-half-year-old child diagnosed with the ...

A rare form of diabetes is emerging in the very first weeks of life, reshaping how doctors think about blood sugar disorders ...

Marci Shelman and Tristan Dederscheck’s “miracle” baby was diagnosed with neonatal Marfan syndrome. After four months in the ...

Dec 16 (Reuters) - U.S. Health ‌Secretary ​Robert F. Kennedy ‌Jr. on Tuesday added two rare ​genetic disorders, Duchenne Muscular Dystrophy and Metachromatic Leukodystrophy, ‍to the federal newborn ...

Rare genetic disorders affect more than 300 million people worldwide, with children making up 70% of those impacted, according to EURORDIS. These conditions often go undiagnosed for years due to ...

Personalized CRISPR cures for children born with rare genetic diseases are now a step closer to being more widely available. Today, the Chan Zuckerberg Initiative (CZI) and the Innovative Genomics ...

When Meenu Hodiwalla gave birth to her son almost three decades ago, she imagined the early days unfolding like they do for most new parents - tiny fingers curling around hers, the baby's eyes ...

This year saw notable progress in head and neck cancers, Huntington's disease, personalized genetic therapy, and heart ...

BioMarin Pharmaceutical said on Friday it would acquire Amicus Therapeutics for about $4.8 billion, in the drugmaker's second ...